Articles, Newsletters, Podcasts, and Video

Better Survival Trends Seen With Spinraza in SMA Children in Sweden

By Marta Figueiredo PhD / 2022-09-02
Posted in

The introduction of Spinraza (nusinersen) as a treatment for spinal muscular atrophy (SMA) in Sweden was associated with trends of improved survival in children diagnosed

more

CADTH: Spinraza Should Not Be Funded for Adults in Canada

By Marisa Wexler MS / 2022-08-31
Posted in

In its final decision, the Canadian Agency for Drugs and Technologies in Health (CADTH) recommended against Spinraza (nusinersen) being reimbursed to treat adults with spinal muscular atrophy (SMA). 

more

Elevated GFAP Levels Linked to More Motor Impairment in SMA

By Marisa Wexler MS / 2022-08-17
Posted in

Higher levels of the glial fibrillary acidic protein (GFAP) in the fluid around the brain and spinal cord are associated with poorer motor function among

more

Initiating Treatment Early Called More Critical Than Therapy Choice

By Marta Figueiredo PhD / 2022-08-03
Posted in

Initiating a disease-modifying therapy (DMT) before the onset of symptoms and at the earliest time possible results in the best outcomes in infants with spinal

more

Spinraza Treatment May Help to Improve Arm Function in Adults

By Marisa Wexler MS / 2022-07-27
Posted in

Among adults with spinal muscular atrophy (SMA) being treated with Spinraza (nusinersen), a decrease in levels of the inflammatory protein YKL-40 in the fluid around

more

The Best Unorthodox Advice From My Doctor

By Alyssa Silva / 2022-07-15
Posted in

When you’re living with a complicated disease such as SMA, it’s half the battle to have a knowledgeable and trustworthy medical team helping to manage

more

Spinraza Improves, Stabilizes SMA-related Motor Function: Study

By Marisa Wexler MS / 2022-07-15
Posted in

Spinraza (nusinersen) treatment was generally well tolerated and led to improved or stabilized motor function for nearly 300 children with spinal muscular atrophy (SMA) in

more

Regular Physical Therapy Linked to Better Results in Spinraza Study

By Marta Figueiredo PhD / 2022-07-13
Posted in

Undergoing physical therapy nearly every day while on Spinraza (nusinersen) leads to significantly greater motor improvements than occasional sessions for children and adolescents with spinal

more

2 Given Spinraza as Newborns Still Showing Normal Development

By Marta Figueiredo PhD / 2022-07-11
Posted in

Two children genetically diagnosed with spinal muscular atrophy (SMA) before birth and starting treatment with Spinraza (nusinersen) within the first days of life have shown normal

more

Australian State Queensland to Screen Newborns for SMA, SCID

By Ana de Barros PhD / 2022-06-27
Posted in

The Australian state of Queensland  is expanding its newborn screening program to include the genetic conditions spinal muscular atrophy (SMA) and severe combined immunodeficiency (SCID).

more